-
Why is she in pain now that her disease has been cured?
US Food and Drug Administration (FDA) approved two gene therapy treatments for sickle-cell disease last year, including the first CRISPR-based genome-editing therapy the agency has ever authorized. Both stem-cell transplants and gene therapy require chemotherapy before the treatment. Three rounds of chemotherapy and other treatments drove her cancer into remission, but she still struggles with…
-
She is in pain after being cured of her disease
A new study has claimed that gene therapy could be used to treat sickle cell disease, a form of blood disorder. According to the study, the gene therapy could delay the spread of the disease and possibly even prevent it. It added that gene therapy could also be used to treat other diseases in which…
-
The race to save a woman’s life consists of hope, despair, and CRISPR
A 20-year-old woman with a rare form of brain disease, Uditi Ghosh, received a gene therapy that she described as a “go-getter”. Uditi, who was diagnosed with a genetic condition called’FENIB’, received CRISPR-Cas9 gene therapy through a vaccine developed by National Institute of Medical Sciences (NIMS). The therapy was given to her by a team…
-
It was the first Crispr Medicine to get approved
US’ Food and Drug Administration approved Crispr Therapeutics’ experimental vaccine Casgevy for the treatment of sickle Cell disease, a blood disorder that causes uncontrollable blood clotting. It is the first-ever “gene therapy” to have been approved for use by the US. According to the company’s preliminary results, 90% of patients didn’t require a red-blood-cell transfusion…
-
The Y chromosome has an effect on cancer risk
Biotech company SanaHeal has won the Spinoff Prize, an award fromNature Research and Merck for early-stage university spin-off companies. SanaHeal was founded in 2014 by Harvard University’s evolutionary biologist Shu Jing and University of Pennsylvania’s computational biologist and genomics professor Charles Ornstein. It will receive $1 million from Nature Research and Merck for its development…
-
A disgraced scientist thinks the editing of human embryos should be banned
Chinese scientist He Jiankui, who made the world’s first COVID-19-resistant baby in 2018, said that he wants to use gene therapy instead of heritable changes to human embryos to help families with rare diseases and other diseases. However, he also wants to use gene therapy to treat people who already have the disease rather than…